Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model (Q34030144)

30 July 2017

title

Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model (English)

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30 July 2017

author

Adrian Robert Krainer

7

object named as

Adrian R Krainer

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30 July 2017

Yimin Hua

1

1 reference

30 July 2017

Kentaro Sahashi

2

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30 July 2017

Gene Hung

3

1 reference

30 July 2017

Frank Rigo

4

1 reference

30 July 2017

Marco A Passini

5

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30 July 2017

C Frank Bennett

6

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30 July 2017

publication date

12 July 2010

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30 July 2017

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30 July 2017

volume

24

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30 July 2017

issue

15

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30 July 2017

page(s)

1634-1644

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Mechanisms underlying inflammation in neurodegeneration

30 July 2017

cites work

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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Restoration of SMN function: delivery of a trans-splicing RNA re-directs SMN2 pre-mRNA splicing

5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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Correction of SMN2 Pre-mRNA splicing by antisense U7 small nuclear RNAs

5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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The human centromeric survival motor neuron gene (SMN2) rescues embryonic lethality in Smn(-/-) mice and results in a mouse with spinal muscular atrophy

5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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Inactivation of the survival motor neuron gene, a candidate gene for human spinal muscular atrophy, leads to massive cell death in early mouse embryos

5 July 2018

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5 July 2018

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Correlation between severity and SMN protein level in spinal muscular atrophy

5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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5 July 2018

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Molecular and phenotypic reassessment of an infrequently used mouse model for spinal muscular atrophy.

5 July 2018

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Control of alternative splicing through siRNA-mediated transcriptional gene silencing.

29 October 2018

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Oligonucleotide-mediated survival of motor neuron protein expression in CNS improves phenotype in a mouse model of spinal muscular atrophy.

29 October 2018

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29 October 2018

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Multiprotein complexes of the survival of motor neuron protein SMN with Gemins traffic to neuronal processes and growth cones of motor neurons

29 October 2018

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29 October 2018

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29 October 2018

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A multiprotein complex mediates the ATP-dependent assembly of spliceosomal U snRNPs

29 October 2018

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International SMA consortium meeting. (26-28 June 1992, Bonn, Germany)

29 October 2018

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12 December 2020

SMNDelta7, the major product of the centromeric survival motor neuron (SMN2) gene, extends survival in mice with spinal muscular atrophy and associates with full-length SMN

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12 December 2020

Finger cold-induced vasodilatation, sympathetic skin response, and R-R interval variation in patients with progressive spinal muscular atrophy

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12 December 2020

Establishing a standardized therapeutic testing protocol for spinal muscular atrophy

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12 December 2020

Identifiers

DOI

10.1101/GAD.1941310

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30 July 2017

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30 July 2017

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