A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia (Q28291035)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

author name string

M. Grossman

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

D. J. Rader

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

D. M. Kolansky

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

K. Kozarsky

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

B. J. Clark

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

E. A. Stein

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

P. J. Lupien

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

H. B. Brewer

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

24 May 2024

S. E. Raper

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A7584986

full work available at URL

24 May 2024

language of work or name

English

0 references

publication date

November 1995

0 references

http://www.nature.com/articles/nm1195-1148

1 reference

https://api.crossref.org/works/10.1038/NM1195-1148

http://www.nature.com/articles/nm1195-1148.pdf

24 May 2024

file format

Portable Document Format

1 reference

https://api.crossref.org/works/10.1038/NM1195-1148

24 May 2024

0 references

1

0 references

issue

11

0 references

page(s)

1148-54

0 references

cites work

Complementarity of colestipol, niacin, and lovastatin in treatment of severe familial hypercholesterolemia

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

Failure of complete bile diversion and oral bile acid therapy in the treatment of homozygous familial hypercholesterolemia

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

Liver transplantation to provide low-density-lipoprotein receptors and lower plasma cholesterol in a child with homozygous familial hypercholesterolemia

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

Liver transplantation for treatment of cardiovascular disease: comparison with medication and plasma exchange in homozygous familial hypercholesterolemia

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

Treatment of refractory familial hypercholesterolemia by low-density lipoprotein apheresis using an automated dextran sulfate cellulose adsorption system. The Liposorber Study Group

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

Defective lipoprotein receptors and atherosclerosis. Lessons from an animal counterpart of familial hypercholesterolemia

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

A receptor-mediated pathway for cholesterol homeostasis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Lovastatin therapy in receptor-negative homozygous familial hypercholesterolemia: Lack of effect on low-density lipoprotein concentrations or turnover

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Portacaval shunt in patients with familial hypercholesterolemia

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Hypercholesterolemia in low density lipoprotein receptor knockout mice and its reversal by adenovirus-mediated gene delivery

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Long-Term Improvement of Hypercholesterolemia After Ex Vivo Gene Therapy in LDLR-Deficient Rabbits

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Transplantation of genetically modified autologous hepatocytes into nonhuman primates: feasibility and short-term toxicity.

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Ex vivo gene therapy of familial hypercholesterolemia.

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

The low density lipoprotein receptor is not required for normal catabolism of Lp(a) in humans

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Towards liver-directed gene therapy: retrovirus-mediated gene transfer into human hepatocytes

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Transduction of primary human hepatocytes with amphotropic and xenotropic retroviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Gene therapy for cholesterol

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Molecular genetics of the LDL receptor gene in familial hypercholesterolemia

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Common low-density lipoprotein receptor mutations in the French Canadian population

1 reference

https://api.crossref.org/works/10.1038%2FNM1195-1148

7 January 2021

Identifiers

DOI

10.1038/NM1195-1148

0 references