A single intravenous rAAV injection as late as P20 achieves efficacious and sustained CNS Gene therapy in Canavan mice. (Q30559496)
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English | A single intravenous rAAV injection as late as P20 achieves efficacious and sustained CNS Gene therapy in Canavan mice. |
scientific article |
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A single intravenous rAAV injection as late as P20 achieves efficacious and sustained CNS Gene therapy in Canavan mice (English)
Seemin Seher Ahmed
Huapeng Li
Chunyan Cao
Elif M Sikoglu
Andrew R Denninger
Qin Su
Samuel Eaton
Ana A Liso Navarro
Jun Xie
Sylvia Szucs
Hongwei Zhang
Constance Moore
Terence R Flotte
Reuben Matalon
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