Combination small molecule PPT1 mimetic and CNS-directed gene therapy as a treatment for infantile neuronal ceroid lipofuscinosis (Q33939283)
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English | Combination small molecule PPT1 mimetic and CNS-directed gene therapy as a treatment for infantile neuronal ceroid lipofuscinosis |
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Combination small molecule PPT1 mimetic and CNS-directed gene therapy as a treatment for infantile neuronal ceroid lipofuscinosis (English)
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Marie S Roberts
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Shannon L Macauley
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Andrew M Wong
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Denis Yilmas
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Sarah Hohm
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Jonathan D Cooper
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Mark S Sands
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7 February 2012
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35
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847-857
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