Meganucleases can restore the reading frame of a mutated dystrophin (Q34110253)

31 July 2017

title

Meganucleases can restore the reading frame of a mutated dystrophin (English)

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31 July 2017

P Chapdelaine

1

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31 July 2017

C Pichavant

2

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31 July 2017

J Rousseau

3

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31 July 2017

F Pâques

4

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31 July 2017

J P Tremblay

5

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31 July 2017

publication date

15 April 2010

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31 July 2017

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31 July 2017

volume

17

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31 July 2017

issue

7

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31 July 2017

page(s)

846-858

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Induction of homologous recombination in mammalian chromosomes by using the I-SceI system of Saccharomyces cerevisiae

31 July 2017

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Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

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Sustained AAV-mediated dystrophin expression in a canine model of Duchenne muscular dystrophy with a brief course of immunosuppression

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Microutrophin delivery through rAAV6 increases lifespan and improves muscle function in dystrophic dystrophin/utrophin-deficient mice

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Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

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Autologous transplantation of SM/C-2.6(+) satellite cells transduced with micro-dystrophin CS1 cDNA by lentiviral vector into mdx mice.

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Mesoangioblast stem cells ameliorate muscle function in dystrophic dogs

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Dystrophin expression in muscles of duchenne muscular dystrophy patients after high-density injections of normal myogenic cells.

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First test of a "high-density injection" protocol for myogenic cell transplantation throughout large volumes of muscles in a Duchenne muscular dystrophy patient: eighteen months follow-up

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PTC124 targets genetic disorders caused by nonsense mutations

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Nanopolymers improve delivery of exon skipping oligonucleotides and concomitant dystrophin expression in skeletal muscle of mdx mice

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Meganucleases and DNA double-strand break-induced recombination: perspectives for gene therapy

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A yeast-endonuclease-generated DNA break induces antigenic switching in Trypanosoma brucei

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Directed evolution and substrate specificity profile of homing endonuclease I-SceI.

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7 January 2021

Computational redesign of endonuclease DNA binding and cleavage specificity

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7 January 2021

Engineering of large numbers of highly specific homing endonucleases that induce recombination on novel DNA targets

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7 January 2021

A combinatorial approach to create artificial homing endonucleases cleaving chosen sequences

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7 January 2021

Molecular basis of xeroderma pigmentosum group C DNA recognition by engineered meganucleases

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7 January 2021

Engineered I-CreI derivatives cleaving sequences from the human XPC gene can induce highly efficient gene correction in mammalian cells

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7 January 2021

Transplantation of myoblasts from a transgenic mouse overexpressing dystrophin produced only a relatively small increase of dystrophin-positive membrane

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7 January 2021

Chromosomal translocations induced at specified loci in human stem cells.

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7 January 2021

Initiation of DNA fragmentation during apoptosis induces phosphorylation of H2AX histone at serine 139

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7 January 2021

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7 January 2021

A canine minidystrophin is functional and therapeutic in mdx mice

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7 January 2021

Protein estimation directly from SDS-PAGE loading buffer for standardization of samples from cell lysates or tissue homogenates before Western blot analysis

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7 January 2021

Nucleofection of muscle-derived stem cells and myoblasts with phiC31 integrase: stable expression of a full-length-dystrophin fusion gene by human myoblasts

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7 January 2021

Identifiers

DOI

10.1038/GT.2010.26

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Dimensions Publication ID

31 July 2017

1023491052

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Fatcat ID

release_o7enqz3dmjgb5iskpcv7nft4tm

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Fatcat

https://api.fatcat.wiki/v0/release/o7enqz3dmjgb5iskpcv7nft4tm

24 November 2022

mapped directly with Wikidata item

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