Gene transfer of human acid sphingomyelinase corrects neuropathology and motor deficits in a mouse model of Niemann-Pick type A disease (Q34202095)
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English | Gene transfer of human acid sphingomyelinase corrects neuropathology and motor deficits in a mouse model of Niemann-Pick type A disease |
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Gene transfer of human acid sphingomyelinase corrects neuropathology and motor deficits in a mouse model of Niemann-Pick type A disease (English)
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Edward H Schuchman
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James C Dodge
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Jennifer Clarke
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Antonius Song
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Jie Bu
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Wendy Yang
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Tatyana V Taksir
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Denise Griffiths
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Michael A Zhao
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Seng H Cheng
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Catherine R O'Riordan
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Lamya S Shihabuddin
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Marco A Passini
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Gregory R Stewart
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21 November 2005
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102
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49
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17822-17827
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