Adeno-associated virus-mediated gene transfer (Q34317131)

1 August 2017

title

Adeno-associated virus-mediated gene transfer (English)

1 reference

1 August 2017

Arun Srivastava

1

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1 August 2017

publication date

1 September 2008

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Journal of Cellular Biochemistry

1 August 2017

published in

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1 August 2017

volume

105

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1 August 2017

issue

1

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1 August 2017

page(s)

17-24

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Next generation of adeno-associated virus 2 vectors: point mutations in tyrosines lead to high-efficiency transduction at lower doses

1 August 2017

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6 July 2018

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Vector integration is nonrandom and clustered and influences the fate of lymphopoiesis in SCID-X1 gene therapy

6 July 2018

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Adeno-associated virus-mediated gene transfer in hematopoietic stem/ progenitor cells as a therapeutic tool

6 July 2018

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Adeno-associated virus 2-mediated gene transfer: role of a cellular serine/threonine protein phosphatase in augmenting transduction efficiency

6 July 2018

1 reference

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Recombinant AAV2 transduction of primitive human hematopoietic stem cells capable of serial engraftment in immune-deficient mice

6 July 2018

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Hematopoietic stem cell transduction by recombinant adeno-associated virus vectors: problems and solutions

6 July 2018

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Adeno-associated viral vectors for clinical gene transfer studies

6 July 2018

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Adeno-associated virus vectors: potential applications for cancer gene therapy

6 July 2018

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Impaired nuclear transport and uncoating limit recombinant adeno-associated virus 2 vector-mediated transduction of primary murine hematopoietic cells.

6 July 2018

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Clades of Adeno-associated viruses are widely disseminated in human tissues.

6 July 2018

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Gene delivery to human and murine primitive hematopoietic stem and progenitor cells by AAV2 vectors

6 July 2018

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Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer

6 July 2018

1 reference

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LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

6 July 2018

1 reference

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American Society of Gene Therapy (ASGT) ad hoc subcommittee on retroviral-mediated gene transfer to hematopoietic stem cells

6 July 2018

1 reference

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AAV serotype 2 vectors preferentially integrate into active genes in mice

6 July 2018

1 reference

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AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

6 July 2018

1 reference

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Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

6 July 2018

1 reference

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Muscle-specific promoters may be necessary for adeno-associated virus-mediated gene transfer in the treatment of muscular dystrophies.

6 July 2018

1 reference

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Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

6 July 2018

1 reference

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Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue

6 July 2018

1 reference

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Transfer of contaminants in adeno-associated virus vector stocks can mimic transduction and lead to artifactual results

6 July 2018

1 reference

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Adeno-associated virus type 2-mediated transduction in primary human bone marrow-derived CD34+ hematopoietic progenitor cells: donor variation and correlation of transgene expression with cellular differentiation.

6 July 2018

1 reference

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High-level globin gene expression mediated by a recombinant adeno-associated virus genome that contains the 3' gamma globin gene regulatory element and integrates as tandem copies in erythroid cells

6 July 2018

1 reference

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Recombinant adeno-associated virus mediates a high level of gene transfer but less efficient integration in the K562 human hematopoietic cell line

6 July 2018

1 reference

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A phase I study of an adeno-associated virus-CFTR gene vector in adult CF patients with mild lung disease

6 July 2018

1 reference

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Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector

6 July 2018

1 reference

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Adeno-associated virus 2-mediated high efficiency gene transfer into immature and mature subsets of hematopoietic progenitor cells in human umbilical cord blood

6 July 2018

1 reference

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Use of adeno-associated virus as a mammalian DNA cloning vector: transduction of neomycin resistance into mammalian tissue culture cells

6 July 2018

1 reference

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Adeno-associated viruses: an update.

6 July 2018

1 reference

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Gene transfer into hematopoietic progenitor cells mediated by an adeno-associated virus vector

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2983091

A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease

6 July 2018

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From crystal structure to clinic: highlights of the Tenth International Parvovirus Workshop

21 January 2018

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No evidence for tumorigenesis of AAV vectors in a large-scale study in mice.

21 January 2018

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Analysis of tumors arising in male B6C3F1 mice with and without AAV vector delivery to liver.

21 January 2018

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AAV vector integration sites in mouse hepatocellular carcinoma.

21 January 2018

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Phase I trial of intramuscular injection of a recombinant adeno-associated virus alpha 1-antitrypsin (rAAV2-CB-hAAT) gene vector to AAT-deficient adults

21 January 2018

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CNS-directed AAV2-mediated gene therapy ameliorates functional deficits in a murine model of infantile neuronal ceroid lipofuscinosis.

21 January 2018

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Stable integration of recombinant adeno-associated virus vector genomes after transduction of murine hematopoietic stem cells.

21 January 2018

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Recombinant self-complementary adeno-associated virus serotype vector-mediated hematopoietic stem cell transduction and lineage-restricted, long-term transgene expression in a murine serial bone marrow transplantation model.

21 January 2018

1 reference

Efficient gene transfer into human cord blood CD34+ cells and the CD34+CD38- subset using highly purified recombinant adeno-associated viral vector preparations that are free of helper virus and wild-type AAV.

21 January 2018

1 reference

Quiescent subpopulations of human CD34-positive hematopoietic stem cells are preferred targets for stable recombinant adeno-associated virus type 2 transduction

21 January 2018

1 reference

Gene therapy with viral vectors: the hope, the problems, and the solution

21 January 2018

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Adeno-associated virus 2-mediated transduction and erythroid lineage-restricted long-term expression of the human beta-globin gene in hematopoietic cells from homozygous beta-thalassemic mice

21 January 2018

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A phase II, double-blind, randomized, placebo-controlled clinical trial of tgAAVCF using maxillary sinus delivery in patients with cystic fibrosis with antrostomies.

21 January 2018

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Self-complementary recombinant adeno-associated viral vectors: packaging capacity and the role of rep proteins in vector purity.

21 January 2018

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Evaluation of primitive murine hematopoietic stem and progenitor cell transduction in vitro and in vivo by recombinant adeno-associated virus vector serotypes 1 through 5.

21 January 2018

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The Genetics of Adeno-Associated Virus

21 January 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2983091

Gene therapeutic prospects in early onset of severe retinal dystrophy: restoration of vision in RPE65 Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium

28 October 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/18500727

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1002/JCB.21819

1 reference

1 August 2017

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1 August 2017

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