Cystic fibrosis transmembrane conductance regulator with a shortened R domain rescues the intestinal phenotype of CFTR-/- mice. (Q34582621)

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21 January 2020

title

Cystic fibrosis transmembrane conductance regulator with a shortened R domain rescues the intestinal phenotype of CFTR-/- mice (English)

1 reference

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21 January 2020

main subject

transmembrane protein

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1

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21 January 2020

David Meyerholz

2

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21 January 2020

Curt D. Sigmund

6

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21 January 2020

author name string

Daniel W Vermeer

3

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21 January 2020

Philip H Karp

4

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21 January 2020

Lindsey Schneider

5

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21 January 2020

Michael J Welsh

7

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21 January 2020

language of work or name

English

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publication date

1 February 2011

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Proceedings of the National Academy of Sciences of the United States of America

21 January 2020

published in

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21 January 2020

volume

108

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21 January 2020

issue

7

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21 January 2020

page(s)

2921-2926

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Pigs and humans with cystic fibrosis have reduced insulin-like growth factor 1 (IGF1) levels at birth

21 January 2020

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A shortened adeno-associated virus expression cassette for CFTR gene transfer to cystic fibrosis airway epithelia.

7 July 2018

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Functional characterization of a recombinant adeno-associated virus 5-pseudotyped cystic fibrosis transmembrane conductance regulator vector

7 July 2018

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CFTR with a partially deleted R domain corrects the cystic fibrosis chloride transport defect in human airway epithelia in vitro and in mouse nasal mucosa in vivo

7 July 2018

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7 July 2018

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Adeno-associated virus type 6 (AAV6) vectors mediate efficient transduction of airway epithelial cells in mouse lungs compared to that of AAV2 vectors

7 July 2018

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A functional R domain from cystic fibrosis transmembrane conductance regulator is predominantly unstructured in solution

7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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Transgenic mice containing intestinal fatty acid-binding protein-human growth hormone fusion genes exhibit correct regional and cell-specific expression of the reporter gene in their small intestine

7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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21 January 2018

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21 January 2018

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27 October 2018

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21 January 2018

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21 January 2018

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12 December 2020

Correction of lethal intestinal defect in a mouse model of cystic fibrosis by human CFTR

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12 December 2020

Processing of CFTR bearing the P574H mutation differs from wild-type and deltaF508-CFTR

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12 December 2020

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12 December 2020

Cellular localization of the cystic fibrosis transmembrane conductance regulator in mouse intestinal tract

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12 December 2020

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12 December 2020

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12 December 2020

Identifiers

DOI

10.1073/PNAS.1019752108

1 reference

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21 January 2020

0 references

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21 January 2020

PubMed publication ID

21285372

1 reference