Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type I (Q34621690)
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English | Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type I |
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Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type I (English)
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Bruce R Blazar
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Gordon Freeman
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Mark J Osborn
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Ron T McElmurry
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Christopher J Lees
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Anthony P DeFeo
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Zhi-Ying Chen
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Mark A Kay
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16 November 2010
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