Preclinical safety evaluation of a recombinant AAV8 vector for X-linked retinoschisis after intravitreal administration in rabbits (Q34768369)

4 August 2017

title

Preclinical safety evaluation of a recombinant AAV8 vector for X-linked retinoschisis after intravitreal administration in rabbits (English)

1 reference

Camasamudram Vijayasarathy

4 August 2017

main subject

X-linked retinoschisis

1 reference

based on heuristic

inferred from title

author

5

object named as

Camasamudram Vijayasarathy

1 reference

4 August 2017

11

Paul A Sieving

1 reference

4 August 2017

8

Ronald A Bush

1 reference

4 August 2017

Dario Marangoni

1

1 reference

4 August 2017

Zhijian Wu

2

1 reference

4 August 2017

Henry E Wiley

3

1 reference

4 August 2017

Caroline J Zeiss

4

1 reference

4 August 2017

Yong Zeng

6

1 reference

4 August 2017

Suja Hiriyanna

7

1 reference

4 August 2017

Lisa L Wei

9

1 reference

4 August 2017

Peter Colosi

10

1 reference

4 August 2017

publication date

1 December 2014

1 reference

Human gene therapy. Clinical development

4 August 2017

published in

1 reference

4 August 2017

volume

25

1 reference

4 August 2017

issue

4

1 reference

4 August 2017

page(s)

202-211

1 reference

Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial.

4 August 2017

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Intravitreal delivery of AAV8 retinoschisin results in cell type-specific gene expression and retinal rescue in the Rs1-KO mouse

7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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RS1, a discoidin domain-containing retinal cell adhesion protein associated with X-linked retinoschisis, exists as a novel disulfide-linked octamer.

7 July 2018

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A retinal neuronal developmental wave of retinoschisin expression begins in ganglion cells during layer formation

7 July 2018

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RS-1 Gene Delivery to an Adult Rs1h Knockout Mouse Model Restores ERG b-Wave with Reversal of the Electronegative Waveform of X-Linked Retinoschisis

7 July 2018

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7 July 2018

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7 July 2018

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Expression of X-linked retinoschisis protein RS1 in photoreceptor and bipolar cells

7 July 2018

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Retinoschisin, the X-linked retinoschisis protein, is a secreted photoreceptor protein, and is expressed and released by Weri-Rb1 cells

7 July 2018

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7 July 2018

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1 reference

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In vivo-directed evolution of a new adeno-associated virus for therapeutic outer retinal gene delivery from the vitreous

7 July 2018

1 reference

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Direct comparison of administration routes for AAV8-mediated ocular gene therapy

26 October 2018

1 reference

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Efficacy of sustained topical dorzolamide therapy for cystic macular lesions in patients with X-linked retinoschisis

26 October 2018

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Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors

26 October 2018

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26 October 2018

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26 October 2018

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26 October 2018

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26 October 2018

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26 October 2018

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26 October 2018

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26 October 2018

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26 October 2018

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RETINAL TOXICITY OF INTRAVITREAL KENALOG IN ALBINO RABBITS

26 October 2018

1 reference

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Long-term Retinal Toxicity of Intravitreal Commercially Available Preserved Triamcinolone Acetonide (Kenalog) in Rabbit Eyes

9 December 2018

1 reference

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Acetazolamide in the treatment of X-linked retinoschisis maculopathy

9 December 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25211193

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1089/HUMC.2014.067

1 reference

4 August 2017

1 reference

4 August 2017

1 reference