Molecular medicine for the brain: silencing of disease genes with RNA interference (Q35674368)

9 August 2017

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title

Molecular medicine for the brain: silencing of disease genes with RNA interference (English)

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9 August 2017

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Beverly L Davidson

1

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PubMed ID

14980529

9 August 2017

Henry L Paulson

series ordinal

2

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PubMed ID

14980529

9 August 2017

language of work or name

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1 March 2004

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9 August 2017

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9 August 2017

3

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9 August 2017

3

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9 August 2017

145-149

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https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

9 August 2017

1 reference

7 January 2021

Approaches for the sequence-specific knockdown of mRNA.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Duplexes of 21-nucleotide RNAs mediate RNA interference in cultured mammalian cells

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

A system for stable expression of short interfering RNAs in mammalian cells

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Asymmetry in the assembly of the RNAi enzyme complex

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Rescue of polyglutamine-mediated cytotoxicity by double-stranded RNA-mediated RNA interference

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Allele-specific silencing of dominant disease genes

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

siRNA-mediated gene silencing in vitro and in vivo.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Toxic proteins in neurodegenerative disease

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Increased apoptosis and early embryonic lethality in mice nullizygous for the Huntington's disease gene homologue

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Inactivation of the mouse Huntington's disease gene homolog Hdh

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Inactivation of Hdh in the brain and testis results in progressive neurodegeneration and sterility in mice

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Allele-specific silencing of a pathogenic mutant acetylcholine receptor subunit by RNA interference

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Selective silencing by RNAi of a dominant allele that causes amyotrophic lateral sclerosis

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Toward therapy for DYT1 dystonia: allele-specific silencing of mutant TorsinA

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Targeting Alzheimer's disease genes with RNA interference: an efficient strategy for silencing mutant alleles

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Genetics of primary dystonia

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Insulin activation of Rheb, a mediator of mTOR/S6K/4E-BP signaling, is inhibited by TSC1 and 2

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

BACE1 Suppression by RNA Interference in Primary Cortical Neurons

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

RNAi functions in cultured mammalian neurons

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Local gene knockdown in the brain using viral-mediated RNA interference.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Expression profiling reveals off-target gene regulation by RNAi

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https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Genomewide view of gene silencing by small interfering RNAs

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

The specifics of small interfering RNA specificity

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Functional correction of established central nervous system deficits in an animal model of lysosomal storage disease with feline immunodeficiency virus-based vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Rabies virus glycoprotein pseudotyping of lentiviral vectors enables retrograde axonal transport and access to the nervous system after peripheral delivery

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

In vivo gene transfer using a nonprimate lentiviral vector pseudotyped with Ross River Virus glycoproteins

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Recombinant adeno-associated virus type 2, 4, and 5 vectors: transduction of variant cell types and regions in the mammalian central nervous system.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

Convection-enhanced delivery of AAV vector in parkinsonian monkeys; in vivo detection of gene expression and restoration of dopaminergic function using pro-drug approach

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2804%2900678-7

7 January 2021

10.1016/S1474-4422(04)00678-7

Identifiers

DOI

1 reference

9 August 2017

1 reference

PubMed ID

14980529