Prevention of Lethal Murine Hypophosphatasia by Neonatal Ex Vivo Gene Therapy Using Lentivirally Transduced Bone Marrow Cells (Q35807632)

10 August 2017

Prevention of Lethal Murine Hypophosphatasia by Neonatal Ex Vivo Gene Therapy Using Lentivirally Transduced Bone Marrow Cells (English)

1 reference

10 August 2017

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5

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Shinichi Abe

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

author name string

Osamu Iijima

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Koichi Miyake

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Atsushi Watanabe

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Noriko Miyake

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Chizu Kanokoda

6

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Aki Nakamura-Takahashi

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Hideaki Kinoshita

8

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Taku Noguchi

9

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Sonoko Narisawa

11

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

José Luis Millán

12

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Takashi Okada

13

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Takashi Shimada

14

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

publication date

15 October 2015

1 reference

10 August 2017

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

volume

26

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

page(s)

801-812

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

issue

12

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26467745%20AND%20SRC:MED&resulttype=core&format=json

Hypophosphatasia: validation and expansion of the clinical nosology for children from 25 years experience with 173 pediatric patients

4 June 2020

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Successful gene therapy in utero for lethal murine hypophosphatasia

27 July 2018

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Rescue of severe infantile hypophosphatasia mice by AAV-mediated sustained expression of soluble alkaline phosphatase

27 July 2018

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Solving the problem of γ-retroviral vectors containing long terminal repeats

27 July 2018

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Prolonged survival and phenotypic correction of Akp2(-/-) hypophosphatasia mice by lentiviral gene therapy

27 July 2018

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Efficacy of gene therapy for X-linked severe combined immunodeficiency

27 July 2018

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Physiological role of alkaline phosphatase explored in hypophosphatasia

27 July 2018

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Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

27 July 2018

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Kinetic analysis of substrate utilization by native and TNAP-, NPP1-, or PHOSPHO1-deficient matrix vesicles

27 July 2018

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27 July 2018

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Optimized lentiviral vector design improves titer and transgene expression of vectors containing the chicken beta-globin locus HS4 insulator element

27 July 2018

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27 July 2018

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Infantile hypophosphatasia: transplantation therapy trial using bone fragments and cultured osteoblasts

27 July 2018

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27 July 2018

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27 July 2018

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27 July 2018

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27 July 2018

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27 July 2018

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Alkaline phosphatase: placental and tissue-nonspecific isoenzymes hydrolyze phosphoethanolamine, inorganic pyrophosphate, and pyridoxal 5'-phosphate. Substrate accumulation in carriers of hypophosphatasia corrects during pregnancy

27 July 2018

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27 July 2018

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27 July 2018

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Hypophosphatasia. Review of 24 cases

27 July 2018

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Ex Vivo Expanded Allogeneic Mesenchymal Stem Cells With Bone Marrow Transplantation Improved Osteogenesis in Infants With Severe Hypophosphatasia

27 July 2018

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Clinical characteristics of perinatal lethal hypophosphatasia: a report of 6 cases

25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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25 September 2018

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Human CD34+ hematopoietic progenitor cell-directed lentiviral-mediated gene therapy in a xenotransplantation model of lysosomal storage disease.

25 September 2018

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Inactivation of two mouse alkaline phosphatase genes and establishment of a model of infantile hypophosphatasia.

25 September 2018

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Treatment of X-linked severe combined immunodeficiency by in utero transplantation of paternal bone marrow

25 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/26467745

12 December 2020

inferred from PubMed ID database lookup

New bone formation by allogeneic mesenchymal stem cell transplantation in a patient with perinatal hypophosphatasia

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/26467745

12 December 2020

inferred from PubMed ID database lookup

Prenatal genetic diagnosis of severe perinatal (lethal) hypophosphatasia

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/26467745

12 December 2020

inferred from PubMed ID database lookup

Identifiers

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30 July 2022

release_iywzjoytpnedjh5iummj6pcf6a

Fatcat ID

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Fatcat

https://api.fatcat.wiki/v0/release/iywzjoytpnedjh5iummj6pcf6a

30 July 2022

https://api.fatcat.wiki/v0/release/iywzjoytpnedjh5iummj6pcf6a

1 reference

30 July 2022

https://api.fatcat.wiki/v0/release/iywzjoytpnedjh5iummj6pcf6a

1 reference

30 July 2022