Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships (Q36134910)

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Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships
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    Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships (English)
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    Nouriya A Al-Sannaa
    Luisa Bay
    Deborah S Barbouth
    Youssef Benhayoun
    Cyril Goizet
    Norberto Guelbert
    Simon A Jones
    Ana Maria Martins
    Chanika Phornphutkul
    Celia Reig
    Rebecca Pleat
    Shari Fallet
    Iva Ivanovska Holder
    7 October 2015

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