Safety and clinical activity of elosulfase alfa in pediatric patients with Morquio A syndrome (mucopolysaccharidosis IVA) less than 5 y. (Q36426886)

14 August 2017

Safety and clinical activity of elosulfase alfa in pediatric patients with Morquio A syndrome (mucopolysaccharidosis IVA) less than 5 y. (English)

1 reference

14 August 2017

3

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1 June 2020

author name string

Simon A Jones

1

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1 June 2020

Martin Bialer

2

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1 June 2020

Ken Martin

4

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1 June 2020

Hui Wang

5

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1 June 2020

Ke Yang

6

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1 June 2020

Adam J Shaywitz

7

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1 June 2020

Paul Harmatz

8

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1 June 2020

language of work or name

English

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publication date

2 September 2015

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14 August 2017

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1 June 2020

volume

78

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1 June 2020

page(s)

717-722

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1 June 2020

issue

6

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Creative Commons Attribution-NonCommercial-NoDerivs 4.0 International

1 June 2020

copyright license

start time

2 September 2015

1 reference

April 2022 Public Data File from Crossref

copyright status

copyrighted

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exact match

https://scigraph.springernature.com/pub.10.1038/pr.2015.169

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cites work

Growth Charts for Individuals with Mucopolysaccharidosis VI (Maroteaux-Lamy Syndrome)

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Multi-domain impact of elosufase alfa in Morquio A syndrome in the pivotal phase III trial

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Molecular testing of 163 patients with Morquio A (Mucopolysaccharidosis IVA) identifies 39 novel GALNS mutations

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Growth in patients with mucopolysaccharidosis type III (Sanfilippo disease).

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Mucopolysaccharidosis IVA: correlation between genotype, phenotype and keratan sulfate levels

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Clinical overview and treatment options for non-skeletal manifestations of mucopolysaccharidosis type IVA

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Mucopolysaccharidosis type IVA (Morquio A disease): clinical review and current treatment

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

2000 CDC Growth Charts for the United States: methods and development

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Clinical longitudinal standards for height, weight, height velocity, weight velocity, and stages of puberty

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

The Morquio A Clinical Assessment Program: baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects.

30 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Growth charts for patients affected with Morquio A disease.

21 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

International Morquio A Registry: clinical manifestation and natural course of Morquio A disease.

21 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Mutation and polymorphism spectrum of the GALNS gene in mucopolysaccharidosis IVA (Morquio A).

21 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4700045

Elosulfase alfa: first global approval

21 September 2018

1 reference

Crossref

https://api.crossref.org/works/10.1038%2FPR.2015.169

Validation of an LC-MS/MS assay for detecting relevant disaccharides from keratan sulfate as a biomarker for Morquio A syndrome

31 March 2020

1 reference

Crossref

https://api.crossref.org/works/10.1038%2FPR.2015.169

31 March 2020

Identifiers

DOI

10.1038/PR.2015.169

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26331768%20AND%20SRC:MED&resulttype=core&format=json

Dimensions Publication ID

1 June 2020

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26331768%20AND%20SRC:MED&resulttype=core&format=json

1 June 2020

1 reference