Mannose receptor-mediated delivery of moss-made α-galactosidase A efficiently corrects enzyme deficiency in Fabry mice (Q36582247)

15 August 2017

Mannose receptor-mediated delivery of moss-made α-galactosidase A efficiently corrects enzyme deficiency in Fabry mice (English)

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15 August 2017

Jin-Song Shen

1

1 reference

15 August 2017

Andreas Busch

2

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15 August 2017

Taniqua S Day

3

1 reference

15 August 2017

Xing-Li Meng

4

1 reference

15 August 2017

Chun I Yu

5

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15 August 2017

Paulina Dabrowska-Schlepp

6

1 reference

15 August 2017

Benjamin Fode

7

1 reference

15 August 2017

Holger Niederkrüger

8

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15 August 2017

Sabrina Forni

9

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15 August 2017

Shuyuan Chen

10

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15 August 2017

Raphael Schiffmann

11

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15 August 2017

Thomas Frischmuth

12

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15 August 2017

Andreas Schaaf

13

1 reference

15 August 2017

27 August 2015

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Journal of Inherited Metabolic Disease

15 August 2017

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15 August 2017

39

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15 August 2017

2

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15 August 2017

293-303

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https://scigraph.springernature.com/pub.10.1007/s10545-015-9886-9

15 August 2017

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9 September 2017

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Mannose 6-phosphate receptor and sortilin mediated endocytosis of α-galactosidase A in kidney endothelial cells

9 September 2017

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Fabry disease, enzyme replacement therapy and the significance of antibody responses

9 September 2017

1 reference

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Efficient uptake of recombinant α-galactosidase A produced with a gene-manipulated yeast by Fabry mice kidneys

9 September 2017

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9 September 2017

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Sex differences of urinary and kidney globotriaosylceramide and lyso-globotriaosylceramide in Fabry mice

9 September 2017

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9 September 2017

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9 September 2017

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9 September 2017

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9 September 2017

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Production of glucocerebrosidase with terminal mannose glycans for enzyme replacement therapy of Gaucher's disease using a plant cell system

9 September 2017

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Effect of mannose chain length on targeting of glucocerebrosidase for enzyme replacement therapy of Gaucher disease

9 September 2017

1 reference

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Correction of the biochemical and functional deficits in fabry mice following AAV8-mediated hepatic expression of alpha-galactosidase A.

9 September 2017

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Cellular and tissue distribution of intravenously administered agalsidase alfa

9 September 2017

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9 September 2017

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Enzyme therapy in mannose receptor-null mucopolysaccharidosis VII mice defines roles for the mannose 6-phosphate and mannose receptors

9 September 2017

1 reference

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Targeting macrophages with baculovirus-produced lysosomal enzymes: implications for enzyme replacement therapy of the glycoprotein storage disorder galactosialidosis

9 September 2017

1 reference

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Posttranslational modification of therapeutic proteins in plants

9 September 2017

1 reference

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A biochemical and pharmacological comparison of enzyme replacement therapies for the glycolipid storage disorder Fabry disease

9 September 2017

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9 September 2017

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9 September 2017

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Fabry disease: preclinical studies demonstrate the effectiveness of alpha-galactosidase A replacement in enzyme-deficient mice

9 September 2017

1 reference

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Infusion of alpha-galactosidase A reduces tissue globotriaosylceramide storage in patients with Fabry disease

9 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4754329

Mannose receptor and its putative ligands in normal murine lymphoid and nonlymphoid organs: In situ expression of mannose receptor by selected macrophages, endothelial cells, perivascular microglia, and mesangial cells, but not dendritic cells

9 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4754329

The mannose receptor is a pattern recognition receptor involved in host defense

9 September 2017

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alpha-Galactosidase A deficient mice: a model of Fabry disease

9 September 2017

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9 September 2017

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Lysosomal delivery of therapeutic enzymes in cell models of Fabry disease

9 September 2017

1 reference

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Safety and efficacy of recombinant human alpha-galactosidase A replacement therapy in Fabry's disease

30 September 2017

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Expression and characterization of glycosylated and catalytically active recombinant human alpha-galactosidase A produced in Pichia pastoris

30 September 2017

1 reference

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30 September 2017

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Blocking hyperactive androgen receptor signaling ameliorates cardiac and renal hypertrophy in Fabry mice.

28 June 2018

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Production in yeast of alpha-galactosidase A, a lysosomal enzyme applicable to enzyme replacement therapy for Fabry disease

20 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4754329

Biodistribution, kinetics, and efficacy of highly phosphorylated and non-phosphorylated beta-glucuronidase in the murine model of mucopolysaccharidosis VII.

20 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4754329

Isolation, characterization, and properties of Saccharomyces cerevisiae mnn mutants with nonconditional protein glycosylation defects

20 September 2018

1 reference

12 December 2020

Enzymatic Defect in Fabry's Disease

1 reference

12 December 2020

Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease

1 reference

12 December 2020

Production of α-L-iduronidase in maize for the potential treatment of a human lysosomal storage disease

1 reference

12 December 2020

Characterization of a chemically modified plant cell culture expressed human α-Galactosidase-A enzyme for treatment of Fabry disease

1 reference

12 December 2020

Distribution of alpha-galactosidase A in normal human kidney and renal accumulation and distribution of recombinant alpha-galactosidase A in Fabry mice

1 reference

12 December 2020

Dermal microvascular endothelial cells express the 180-kDa macrophage mannose receptor in situ and in vitro

1 reference

12 December 2020

10.1007/S10545-015-9886-9

Identifiers

DOI

1 reference

15 August 2017

1 reference

15 August 2017

1 reference