Enzyme replacement therapy for treating mucopolysaccharidosis type IVA (Morquio A syndrome): effect and limitations. (Q36677856)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26973801%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

title

Enzyme replacement therapy for treating mucopolysaccharidosis type IVA (Morquio A syndrome): effect and limitations (English)

1 reference

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enzyme replacement therapy

10 March 2020

main subject

0 references

mucopolysaccharidosis type IVA

1 reference

4

1 reference

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10 March 2020

Carlos J Alméciga-Díaz

9

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10 March 2020

author name string

Shunji Tomatsu

1

1 reference

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10 March 2020

Kazuki Sawamoto

2

1 reference

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10 March 2020

Tsutomu Shimada

3

1 reference

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10 March 2020

Francyne Kubaski

5

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10 March 2020

Eriko Yasuda

6

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10 March 2020

Robert W Mason

7

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10 March 2020

Shaukat Khan

8

1 reference

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10 March 2020

Luis A Barrera

10

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10 March 2020

William G Mackenzie

11

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10 March 2020

Tadao Orii

12

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10 March 2020

publication date

29 October 2015

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Expert opinion on orphan drugs

10 March 2020

published in

1 reference

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10 March 2020

volume

3

1 reference

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10 March 2020

issue

11

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10 March 2020

page(s)

1279-1290

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Human recombinant lysosomal enzymes produced in microorganisms.

10 March 2020

cites work

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Long circulating enzyme replacement therapy rescues bone pathology in mucopolysaccharidosis VII murine model

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Immune tolerance improves the efficacy of enzyme replacement therapy in canine mucopolysaccharidosis I.

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Fetal presentation of Morquio disease type A

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10.1517/21678707.2015.1086640

Identifiers

DOI

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10 March 2020

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10 March 2020

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