Progress and prospects: gene therapy for inherited immunodeficiencies (Q37602522)

21 August 2017

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title

Progress and prospects: gene therapy for inherited immunodeficiencies (English)

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21 August 2017

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W Qasim

1

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21 August 2017

H B Gaspar

series ordinal

2

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21 August 2017

A J Thrasher

series ordinal

3

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21 August 2017

publication date

24 September 2009

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21 August 2017

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21 August 2017

volume

16

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21 August 2017

issue

11

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21 August 2017

page(s)

1285-1291

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Somatic mosaicism in primary immune deficiencies

21 August 2017

cites work

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https://api.crossref.org/works/10.1038%2FGT.2009.127

Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Vector integration is nonrandom and clustered and influences the fate of lymphopoiesis in SCID-X1 gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Gammaretrovirus-mediated correction of SCID-X1 is associated with skewed vector integration site distribution in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Gene therapy for severe combined immunodeficiency: are we there yet?

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Gene therapy improves immune function in preadolescents with X-linked severe combined immunodeficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansion

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Prolonged pancytopenia in a gene therapy patient with ADA-deficient SCID and trisomy 8 mosaicism: a case report

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Recent advances in gene therapy for severe congenital immunodeficiency diseases

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Stable and functional lymphoid reconstitution in artemis-deficient mice following lentiviral artemis gene transfer into hematopoietic stem cells.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Successful treatment of canine leukocyte adhesion deficiency by foamy virus vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Allogeneic hematopoietic stem-cell transplantation for leukocyte adhesion deficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Physiological promoters reduce the genotoxic risk of integrating gene vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Vector design for expression of O6-methylguanine-DNA methyltransferase in hematopoietic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Self-inactivating gammaretroviral vectors for gene therapy of X-linked severe combined immunodeficiency.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Meganucleases and DNA double-strand break-induced recombination: perspectives for gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Molecular basis of xeroderma pigmentosum group C DNA recognition by engineered meganucleases

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

Long-term T-cell reconstitution after hematopoietic stem-cell transplantation in primary T-cell-immunodeficient patients is associated with myeloid chimerism and possibly the primary disease phenotype

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

inferred from DOI database lookup

7 January 2021

based on heuristic

Insertional transformation of hematopoietic cells by self-inactivating lentiviral and gammaretroviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.127

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1038/GT.2009.127

1 reference

release_4lsi5yqk4beytlt7iivza6wjfe

21 August 2017

Fatcat ID

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/4lsi5yqk4beytlt7iivza6wjfe

mapped directly with Wikidata item

24 November 2022

based on heuristic

1 reference