Targeted Repair of CYBB in X-CGD iPSCs Requires Retention of Intronic Sequences for Expression and Functional Correction (Q38718308)

http://europepmc.org/abstract/PMC/5368476

10 June 2018

title

Targeted Repair of CYBB in X-CGD iPSCs Requires Retention of Intronic Sequences for Expression and Functional Correction (English)

1 reference

http://europepmc.org/abstract/PMC/5368476

10 June 2018

author

Jizhong Zou

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28153086%20AND%20SRC:MED&resulttype=core&format=json

11 June 2020

Sandra Burkett

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28153086%20AND%20SRC:MED&resulttype=core&format=json

11 June 2020

Harry Malech

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28153086%20AND%20SRC:MED&resulttype=core&format=json

11 June 2020

9

Suk See De Ravin

1 reference

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11 June 2020

author name string

Colin L Sweeney

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28153086%20AND%20SRC:MED&resulttype=core&format=json

11 June 2020

Uimook Choi

3

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11 June 2020

Randall K Merling

4

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11 June 2020

Alexander Liu

5

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11 June 2020

Aaron Bodansky

6

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11 June 2020

Jung-Woong Kim

8

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11 June 2020

publication date

1 February 2017

1 reference

http://europepmc.org/abstract/PMC/5368476

10 June 2018

published in

Molecular Therapy

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11 June 2020

volume

25

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11 June 2020

issue

2

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11 June 2020

page(s)

321-330

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28153086%20AND%20SRC:MED&resulttype=core&format=json

Targeted gene addition in human CD34(+) hematopoietic cells for correction of X-linked chronic granulomatous disease

11 June 2020

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1 reference

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23 June 2018

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23 June 2018

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Successful Combination of Sequential Gene Therapy and Rescue Allo-HSCT in Two Children with X-CGD - Importance of Timing

23 June 2018

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Regulation of CYBB Gene Expression in Human Phagocytes by a Distant Upstream NF-κB Binding Site

23 June 2018

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Hematopoietic specification from human pluripotent stem cells: current advances and challenges toward de novo generation of hematopoietic stem cells

23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity

23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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Oxidase-deficient neutrophils from X-linked chronic granulomatous disease iPS cells: functional correction by zinc finger nuclease-mediated safe harbor targeting

23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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Biochemical correction of X-CGD by a novel chimeric promoter regulating high levels of transgene expression in myeloid cells

23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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23 June 2018

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31 August 2018

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Concentrated RD114-pseudotyped MFGS-gp91phox vector achieves high levels of functional correction of the chronic granulomatous disease oxidase defect in NOD/SCID/beta -microglobulin-/- repopulating mobilized human peripheral blood CD34+ cells

31 August 2018

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Equal potency of gammaretroviral and lentiviral SIN vectors for expression of O6-methylguanine-DNA methyltransferase in hematopoietic cells

31 August 2018

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Crossref

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2016.11.012

10.1016/J.YMTHE.2016.11.012

7 January 2021

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28153086%20AND%20SRC:MED&resulttype=core&format=json

11 June 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28153086%20AND%20SRC:MED&resulttype=core&format=json

11 June 2020

PubMed publication ID

28153086

1 reference