MicroRNA-150-regulated vectors allow lymphocyte-sparing transgene expression in hematopoietic gene therapy (Q39462857)

12 September 2017

title

MicroRNA-150-regulated vectors allow lymphocyte-sparing transgene expression in hematopoietic gene therapy (English)

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12 September 2017

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B Gentner

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Nico Lachmann

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N Lachmann

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Tobias Cantz

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T Cantz

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author name string

J Jagielska

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D Heckl

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S Brennig

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N Pfaff

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T Maetzig

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U Modlich

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A Schambach

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T Moritz

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publication date

6 October 2011

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volume

19

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issue

9

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page(s)

915-924

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Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

12 September 2017

cites work

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Stem-cell gene therapy for the Wiskott-Aldrich syndrome

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Gene therapy of X-linked severe combined immunodeficiency

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Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

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Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion

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A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction

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Pathogenesis of leukodystrophy for Krabbe disease: molecular mechanism and clinical treatment

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Regulatable gene expression systems for gene therapy applications: progress and future challenges

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Lentiviral gene transfer regenerates hematopoietic stem cells in a mouse model for Mpl-deficient aplastic anemia

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Endogenous microRNA can be broadly exploited to regulate transgene expression according to tissue, lineage and differentiation state

21 January 2018

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Exploiting and antagonizing microRNA regulation for therapeutic and experimental applications

21 January 2018

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Absolute quantification of microRNAs by using a universal reference

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Comprehensive microRNA expression profiling of the hematopoietic hierarchy

21 January 2018

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Endogenous microRNA regulation suppresses transgene expression in hematopoietic lineages and enables stable gene transfer

21 January 2018

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A microRNA-regulated lentiviral vector mediates stable correction of hemophilia B mice

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Identification of hematopoietic stem cell-specific miRNAs enables gene therapy of globoid cell leukodystrophy

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Gene transfer of cytidine deaminase protects myelopoiesis from cytidine analogs in an in vivo murine transplant model

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MicroRNA profiling of the murine hematopoietic system

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Ordered progression of stage-specific miRNA profiles in the mouse B2 B-cell lineage

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MiR-150 controls B cell differentiation by targeting the transcription factor c-Myb

21 January 2018

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Dynamic regulation of miRNA expression in ordered stages of cellular development.

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

MicroRNAs modulate hematopoietic lineage differentiation

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

Hematopoietic-specific microRNA expression in human cells

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

microRNA122-regulated transgene expression increases specificity of cardiac gene transfer upon intravenous delivery of AAV9 vectors

21 January 2018

1 reference

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Induction of immune tolerance to FIX following muscular AAV gene transfer is AAV-dose/FIX-level dependent

21 January 2018

1 reference

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Liver-specific microRNA-122 target sequences incorporated in AAV vectors efficiently inhibits transgene expression in the liver

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

miR-181a is an intrinsic modulator of T cell sensitivity and selection

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

miR-150, a microRNA expressed in mature B and T cells, blocks early B cell development when expressed prematurely

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

The role of microRNA-150 as a tumor suppressor in malignant lymphoma

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

MicroRNA-mediated control of cell fate in megakaryocyte-erythrocyte progenitors

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

Platelet microRNA-mRNA coexpression profiles correlate with platelet reactivity.

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

Insertional transformation of hematopoietic cells by self-inactivating lentiviral and gammaretroviral vectors

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

Mechanisms controlling titer and expression of bidirectional lentiviral and gammaretroviral vectors.

21 January 2018

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Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

Plat-E: an efficient and stable system for transient packaging of retroviruses

21 January 2018

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Lentiviral vectors pseudotyped with murine ecotropic envelope: increased biosafety and convenience in preclinical research

21 January 2018

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A virus-encoded inhibitor that blocks RNA interference in mammalian cells

21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2011.148

Murine hematopoietic stem cells change their surface phenotype during ex vivo expansion

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.148

21 January 2018

Identifiers

DOI

10.1038/GT.2011.148

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12 September 2017

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