In vivo post-transcriptional gene silencing of alpha-1 antitrypsin by adeno-associated virus vectors expressing siRNA. (Q40115238)

17 September 2017

In vivo post-transcriptional gene silencing of alpha-1 antitrypsin by adeno-associated virus vectors expressing siRNA. (English)

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17 September 2017

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Martha Campbell-Thompson

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17 September 2017

Jeffrey H Teckman

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author name string

Pedro E Cruz

1

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17 September 2017

Christian Mueller

2

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17 September 2017

Travis L Cossette

3

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17 September 2017

Alexandra Golant

4

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17 September 2017

Qiushi Tang

5

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17 September 2017

Stuart G Beattie

6

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17 September 2017

Mark Brantly

7

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17 September 2017

Keith S Blomenkamp

9

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17 September 2017

Terence R Flotte

11

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17 September 2017

25 June 2007

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17 September 2017

Laboratory Investigation

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17 September 2017

87

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17 September 2017

893-902

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17 September 2017

9

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https://scigraph.springernature.com/pub.10.1038/labinvest.3700629

17 September 2017

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High-level transgene expression in nonhuman primate liver with novel adeno-associated virus serotypes containing self-complementary genomes

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7 January 2021

Liver transduction with recombinant adeno-associated virus is primarily restricted by capsid serotype not vector genotype

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7 January 2021

Functional anatomy of siRNAs for mediating efficient RNAi in Drosophila melanogaster embryo lysate

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7 January 2021

Analyses of hepatocellular proliferation in a mouse model of alpha-1-antitrypsin deficiency

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7 January 2021

Indomethacin increases liver damage in a murine model of liver injury from alpha-1-antitrypsin deficiency

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7 January 2021

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7 January 2021

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7 January 2021

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Identifiers

DOI

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17 September 2017

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