AAV-mediated knockdown of peripherin-2 in vivo using miRNA-based hairpins (Q43221778)

16 November 2017

title

AAV-mediated knockdown of peripherin-2 in vivo using miRNA-based hairpins (English)

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16 November 2017

3

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16 November 2017

A Georgiadis

1

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16 November 2017

M Tschernutter

2

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16 November 2017

S J Robbie

4

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16 November 2017

J McIntosh

5

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16 November 2017

A C Nathwani

6

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16 November 2017

A J Smith

7

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16 November 2017

R R Ali

8

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16 November 2017

publication date

10 December 2009

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16 November 2017

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16 November 2017

volume

17

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16 November 2017

issue

4

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16 November 2017

page(s)

486-493

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https://scigraph.springernature.com/pub.10.1038/gt.2009.162

16 November 2017

exact match

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cites work

Molecular genetics and prospects for therapy of the inherited retinal dystrophies

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Perspective on genes and mutations causing retinitis pigmentosa

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On the genetics of retinitis pigmentosa and on mutation-independent approaches to therapeutic intervention

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Prospects for retinal gene replacement therapy.

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The retinal degeneration slow (rds) gene product is a photoreceptor disc membrane-associated glycoprotein.

21 January 2018

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The spectrum of retinal dystrophies caused by mutations in the peripherin/RDS gene

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21 January 2018

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Prevalence of mutations causing retinitis pigmentosa and other inherited retinopathies

21 January 2018

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Prevalence of disease-causing mutations in families with autosomal dominant retinitis pigmentosa: a screen of known genes in 200 families

21 January 2018

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Effect of gene therapy on visual function in Leber's congenital amaurosis

21 January 2018

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Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial

21 January 2018

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Safety and efficacy of gene transfer for Leber's congenital amaurosis

21 January 2018

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Assessing adenoviral hammerhead ribozyme and small hairpin RNA cassettes in neurons: inhibition of endogenous caspase-3 activity and protection from apoptotic cell death.

21 January 2018

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Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme.

21 January 2018

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Ribozyme rescue of photoreceptor cells in P23H transgenic rats: long-term survival and late-stage therapy.

21 January 2018

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Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa.

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Suppression of mouse rhodopsin expression in vivo by AAV mediated siRNA delivery

21 January 2018

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RNA interference-mediated suppression and replacement of human rhodopsin in vivo

21 January 2018

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A transgenic mouse model for gene therapy of rhodopsin-linked Retinitis Pigmentosa

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RNAi-based suppression and replacement of rds-peripherin in retinal organotypic culture

21 January 2018

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Therapeutic benefit derived from RNAi-mediated ablation of IMPDH1 transcripts in a murine model of autosomal dominant retinitis pigmentosa (RP10).

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Improved retinal function in a mouse model of dominant retinitis pigmentosa following AAV-delivered gene therapy

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Fatality in mice due to oversaturation of cellular microRNA/short hairpin RNA pathways

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Expression profiling reveals off-target gene regulation by RNAi

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MicroRNA precursors in motion: exportin-5 mediates their nuclear export

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Artificial miRNAs mitigate shRNA-mediated toxicity in the brain: implications for the therapeutic development of RNAi

21 January 2018

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An efficient method to enhance gene silencing by using precursor microRNA designed small hairpin RNAs

21 January 2018

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Artificial microRNAs as siRNA shuttles: improved safety as compared to shRNAs in vitro and in vivo

21 January 2018

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Towards mutation-independent silencing of genes involved in retinal degeneration by RNA interference

21 January 2018

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Enhanced gene silencing of HIV-1 specific siRNA using microRNA designed hairpins

21 January 2018

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Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy.

21 January 2018

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Rapid and stable knockdown of an endogenous gene in retinal pigment epithelium

21 January 2018

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RNAi suppresses polyglutamine-induced neurodegeneration in a model of spinocerebellar ataxia.

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21 January 2018

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Gene transfer into the mouse retina mediated by an adeno-associated viral vector

21 January 2018

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Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy

21 January 2018

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Preferential silencing of a common dominant rhodopsin mutation does not inhibit retinal degeneration in a transgenic model

21 January 2018

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Molecular genetics of macular degeneration

21 January 2018

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7 January 2021

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Identifiers

DOI

10.1038/GT.2009.162

1 reference

Dimensions Publication ID

16 November 2017

1004432217

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Fatcat ID

release_m24w6z66grhvnbxnhiurlhxyvq

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Fatcat

https://api.fatcat.wiki/v0/release/m24w6z66grhvnbxnhiurlhxyvq

mapped directly with Wikidata item

24 November 2022

based on heuristic

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