Rescue administration of a helper-dependent adenovirus vector with long-term efficacy in dogs with glycogen storage disease type Ia. (Q44199828)

30 November 2017

Rescue administration of a helper-dependent adenovirus vector with long-term efficacy in dogs with glycogen storage disease type Ia. (English)

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30 November 2017

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glycogen storage disease

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B Crane

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X Luo

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A Demaster

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K D Williams

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D M Kozink

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P Zhang

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T T Brown

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C R Pinto

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K Oka

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F Sun

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M W Jackson

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L Chan

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D D Koeberl

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9 June 2011

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4

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443-452

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https://scigraph.springernature.com/pub.10.1038/gt.2011.86

30 November 2017

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cites work

Type I glycogen storage diseases: disorders of the glucose-6-phosphatase complex

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Glycogen storage disease type Ia in two littermate Maltese puppies.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Canine model and genomic structural organization of glycogen storage disease type Ia (GSD Ia).

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Gene therapy for type I glycogen storage diseases

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

AAV vector-mediated reversal of hypoglycemia in canine and murine glycogen storage disease type Ia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Adeno-associated virus-mediated correction of a canine model of glycogen storage disease type Ia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Progress and prospects: gene therapy for genetic diseases with helper-dependent adenoviral vectors.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

High doses of a helper-dependent adenoviral vector yield supraphysiological levels of alpha1-antitrypsin with negligible toxicity

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Improved hepatic transduction, reduced systemic vector dissemination, and long-term transgene expression by delivering helper-dependent adenoviral vectors into the surgically isolated liver of nonhuman primates.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Efficient, long-term hepatic gene transfer using clinically relevant HDAd doses by balloon occlusion catheter delivery in nonhuman primates

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Lifetime correction of genetic deficiency in mice with a single injection of helper-dependent adenoviral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Helper-dependent adenoviral gene therapy mediates long-term correction of the clotting defect in the canine hemophilia A model

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Isolation and nucleotide sequence of canine glucose-6-phosphatase mRNA: identification of mutation in puppies with glycogen storage disease type Ia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Type I glycogen storage disease: kidney involvement, pathogenesis and its treatment

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Complete normalization of hepatic G6PC deficiency in murine glycogen storage disease type Ia using gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Efficacy of helper-dependent adenovirus vector-mediated gene therapy in murine glycogen storage disease type Ia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Liver transplantation for glycogen storage disease types I, III, and IV

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Neonatal helper-dependent adenoviral vector gene therapy mediates correction of hemophilia A and tolerance to human factor VIII

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Normoglycemia alone is insufficient to prevent long-term complications of hepatocellular adenoma in glycogen storage disease type Ib mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Long-term stable correction of low-density lipoprotein receptor-deficient mice with a helper-dependent adenoviral vector expressing the very low-density lipoprotein receptor

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Low-density lipoprotein receptor gene therapy using helper-dependent adenovirus produces long-term protection against atherosclerosis in a mouse model of familial hypercholesterolemia

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

A helper-dependent adenovirus vector system: removal of helper virus by Cre-mediated excision of the viral packaging signal

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Use of helper-dependent adenoviral vectors of alternative serotypes permits repeat vector administration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

Nutritional goals in glycogen storage disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

7 January 2021

Metabolic control and renal dysfunction in type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

7 January 2021

Renal disease in type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

7 January 2021

Cornstarch regimens for nocturnal treatment of young adults with type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

7 January 2021

Resection of hepatocellular adenoma in patients with glycogen storage disease type Ia

1 reference

https://api.crossref.org/works/10.1038%2FGT.2011.86

7 January 2021

Identifiers

DOI

10.1038/GT.2011.86

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Dimensions Publication ID

30 November 2017

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