Widespread correction of lysosomal storage following intrahepatic injection of a recombinant adeno-associated virus in the adult MPS VII mouse (Q45595051)

From Wikidata

Jump to navigation Jump to search

scientific article published in September 2004

Language	Label	Description	Also known as
English	Widespread correction of lysosomal storage following intrahepatic injection of a recombinant adeno-associated virus in the adult MPS VII mouse	scientific article published in September 2004

Statements

scholarly article

1 reference

Europe PubMed Central

14 December 2017

Widespread correction of lysosomal storage following intrahepatic injection of a recombinant adeno-associated virus in the adult MPS VII mouse (English)

1 reference

Europe PubMed Central

14 December 2017

author name string

Thomas J Sferra

1

1 reference

Europe PubMed Central

14 December 2017

Kristin Backstrom

2

1 reference

Europe PubMed Central

14 December 2017

Chuansong Wang

3

1 reference

Europe PubMed Central

14 December 2017

Rachel Rennard

4

1 reference

Europe PubMed Central

14 December 2017

Matt Miller

5

1 reference

Europe PubMed Central

14 December 2017

Yan Hu

6

1 reference

Europe PubMed Central

14 December 2017

publication date

1 September 2004

1 reference

Europe PubMed Central

14 December 2017

Molecular Therapy

1 reference

Europe PubMed Central

14 December 2017

10

1 reference

Europe PubMed Central

14 December 2017

3

1 reference

Europe PubMed Central

14 December 2017

478-491

1 reference

Europe PubMed Central

14 December 2017

Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Enzyme replacement therapy for the mucopolysaccharide storage disorders

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Beta glucuronidase deficiency: report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Murine mucopolysaccharidosis VIL: impact of therapies on the phenotype, clinical course, and pathology in a model of a lysosomal storage disease

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

A single-base-pair deletion in the beta-glucuronidase gene accounts for the phenotype of murine mucopolysaccharidosis type VII

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Structure and function of the mannose 6-phosphate/insulinlike growth factor II receptors

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Mannose 6-phosphate receptors in sorting and transport of lysosomal enzymes

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Delivery of a retroviral vector expressing human beta-glucuronidase to the liver and spleen decreases lysosomal storage in mucopolysaccharidosis VII mice

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Adenovirus-mediated gene transfer and expression of human beta-glucuronidase gene in the liver, spleen, and central nervous system in mucopolysaccharidosis type VII mice

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Adenovirus-mediated gene therapy for mucopolysaccharidosis VII: involvement of cross-correction in wide-spread distribution of the gene products and long-term effects of CTLA-4Ig coexpression

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

The HIV Tat protein transduction domain improves the biodistribution of beta-glucuronidase expressed from recombinant viral vectors.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Prolongation of transgene expression by coexpression of cytokine response modifier a in rodent liver after adenoviral gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Highly purified recombinant adeno-associated virus vectors are biologically active and free of detectable helper and wild-type viruses

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Treatment of a lysosomal storage disease, mucopolysaccharidosis VII, with microencapsulated recombinant cells

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Factors influencing in vivo transduction by recombinant adeno-associated viral vectors expressing the human factor IX cDNA.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Improved hepatic gene transfer by using an adeno-associated virus serotype 5 vector

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Retroviral gene transfer into the intestinal epithelium

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Nonrandom transduction of recombinant adeno-associated virus vectors in mouse hepatocytes in vivo: cell cycling does not influence hepatocyte transduction

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Selective repopulation of normal mouse liver by hepatocytes transduced in vivo with recombinant adeno-associated virus

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

A limited number of transducible hepatocytes restricts a wide-range linear vector dose response in recombinant adeno-associated virus-mediated liver transduction

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Active site mutant transgene confers tolerance to human beta-glucuronidase without affecting the phenotype of MPS VII mice.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Induction of tolerance to human factor VIII in mice

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Abnormal immune function in vivo in a murine model of lysosomal storage disease

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

DNA determinants of structural and regulatory variation within the murine beta-glucuronidase gene complex

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Genomic organization and sequence of the Gus-s alpha allele of the murine beta-glucuronidase gene

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Cell lines for the production of recombinant adeno-associated virus

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Gene transfer to the intestinal tract: a new approach using selective injection of the superior mesenteric artery.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.029

7 January 2021

Identifiers

10.1016/J.YMTHE.2004.05.029

1 reference

Europe PubMed Central

14 December 2017

1 reference

Europe PubMed Central

14 December 2017

ResearchGate publication ID

0 references

Sitelinks

Wikipedia(0 entries)

Wikibooks(0 entries)

Wikinews(0 entries)

Wikiquote(0 entries)

Wikisource(0 entries)

Wikiversity(0 entries)

Wikivoyage(0 entries)

Wiktionary(0 entries)

Multilingual sites(0 entries)

Retrieved from "https://www.wikidata.org/w/index.php?title=Q45595051&oldid=2077427029"