Mechanisms of distribution of mouse beta-galactosidase in the adult GM1-gangliosidosis brain (Q45880488)

17 December 2017

title

Mechanisms of distribution of mouse beta-galactosidase in the adult GM1-gangliosidosis brain (English)

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17 December 2017

author name string

M L D Broekman

1

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17 December 2017

L A Tierney

2

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17 December 2017

C Benn

3

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17 December 2017

P Chawla

4

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17 December 2017

J H Cha

5

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17 December 2017

M Sena-Esteves

6

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17 December 2017

publication date

25 September 2008

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17 December 2017

published in

Gene Therapy

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17 December 2017

volume

16

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17 December 2017

issue

2

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17 December 2017

page(s)

303-308

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17 December 2017

Generalized gangliosidosis: beta-galactosidase deficiency.

cites work

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Gene therapy for lysosomal storage diseases.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Intraventricular brain injection of adeno-associated virus type 1 (AAV1) in neonatal mice results in complementary patterns of neuronal transduction to AAV2 and total long-term correction of storage lesions in the brains of beta-glucuronidase-defici

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Long-term and significant correction of brain lesions in adult mucopolysaccharidosis type VII mice using recombinant AAV vectors.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

In vivo gene therapy of metachromatic leukodystrophy by lentiviral vectors: correction of neuropathology and protection against learning impairments in affected mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of β-glucuronidase

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Functional correction of CNS phenotypes in a lysosomal storage disease model using adeno-associated virus type 4 vectors.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Axons mediate the distribution of arylsulfatase A within the mouse hippocampus upon gene delivery.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Intraventricular enzyme replacement improves disease phenotypes in a mouse model of late infantile neuronal ceroid lipofuscinosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

An autoradiographic study of the organization of intrahippocampal association pathways in the rat

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

The three-dimensional organization of the hippocampal formation: a review of anatomical data

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

The connections of presubiculum and parasubiculum in the rat

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Afferent projections to the mammillary complex of the rat, with special reference to those from surrounding hypothalamic regions

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

alpha-L-Iduronidase transport in neurites.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

An experimental analysis of the efferent projection of the hippocampus

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

AAV vector-mediated correction of brain pathology in a mouse model of Niemann-Pick A disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

RNA trafficking in axons.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

Distribution of a lysosomal enzyme in the adult brain by axonal transport and by cells of the rostral migratory stream.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

7 January 2021

Intravitreal gene therapy reduces lysosomal storage in specific areas of the CNS in mucopolysaccharidosis VII mice.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

7 January 2021

Intrathecal administration of AAV vectors for the treatment of lysosomal storage in the brains of MPS I mice

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

7 January 2021

Generalized CNS disease and massive GM1-ganglioside accumulation in mice defective in lysosomal acid beta-galactosidase

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

7 January 2021

Evidence for collateral projections by neurons in Ammon's horn, the dentate gyrus, and the subiculum: a multiple retrograde labeling study in the rat

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

7 January 2021

On the termination of some afferents to the hippocampus and fascia dentata; an experimental study in the rat.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

7 January 2021

Polyribosomes associated with synaptic specializations on axon initial segments: localization of protein-synthetic machinery at inhibitory synapses

1 reference

https://api.crossref.org/works/10.1038%2FGT.2008.149

7 January 2021

Identifiers

DOI

10.1038/GT.2008.149

1 reference

17 December 2017

Dimensions Publication ID

1020017017

0 references

1 reference

17 December 2017