Toward a gene therapy for dominant disease: validation of an RNA interference-based mutation-independent approach (Q45884385)

17 December 2017

title

Toward a gene therapy for dominant disease: validation of an RNA interference-based mutation-independent approach (English)

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17 December 2017

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author name string

Anna-Sophia Kiang

1

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Arpad Palfi

2

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Paul F Kenna

4

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Sophia Millington-Ward

5

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Gerry Clark

6

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Avril Kennan

7

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Mary O'reilly

8

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Lawrence C T Tam

9

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Aileen Aherne

10

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Niamh McNally

11

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Pete Humphries

12

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G Jane Farrar

13

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publication date

1 September 2005

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17 December 2017

published in

Molecular Therapy

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volume

12

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issue

3

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page(s)

555-561

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Strategems in vitro for gene therapies directed to dominant mutations

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7 January 2021

Identifiers

DOI

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17 December 2017

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17 December 2017