Cell-penetrating peptide-conjugated antisense oligonucleotides restore systemic muscle and cardiac dystrophin expression and function. (Q46375612)

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14 January 2020

title

Cell-penetrating peptide-conjugated antisense oligonucleotides restore systemic muscle and cardiac dystrophin expression and function (English)

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14 January 2020

3

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14 January 2020

Matthew J. Wood

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14 January 2020

author name string

HaiFang Yin

1

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14 January 2020

Hong M Moulton

2

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14 January 2020

Corinne Boyd

4

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14 January 2020

Jordan Boutilier

5

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14 January 2020

Patrick Iverson

6

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publication date

10 September 2008

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14 January 2020

published in

Human Molecular Genetics

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14 January 2020

volume

17

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issue

24

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14 January 2020

page(s)

3909-3918

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Function and genetics of dystrophin and dystrophin-related proteins in muscle

14 January 2020

cites work

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Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

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Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

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12 December 2020

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12 December 2020

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12 December 2020

Adeno-associated virus vector gene transfer and sarcolemmal expression of a 144 kDa micro-dystrophin effectively restores the dystrophin-associated protein complex and inhibits myofibre degeneration in nude/mdx mice

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rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice.

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12 December 2020

Increasing complexity of the dystrophin-associated protein complex

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12 December 2020

Mdx mice inducibly expressing dystrophin provide insights into the potential of gene therapy for duchenne muscular dystrophy

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12 December 2020

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12 December 2020

Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense

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12 December 2020

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12 December 2020

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12 December 2020

Cell-penetrating peptides as transporters for morpholino oligomers: effects of amino acid composition on intracellular delivery and cytotoxicity

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