Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome. (Q51661989)

http://europepmc.org/abstract/MED/27380995

9 April 2018

title

Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome. (English)

1 reference

http://europepmc.org/abstract/MED/27380995

9 April 2018

main subject

enzyme replacement therapy

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author

John J. Mitchell

7

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27380995%20AND%20SRC:MED&resulttype=core&format=json

10 June 2020

Kenneth I. Berger

12

1 reference

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10 June 2020

Chris Hendriksz

1

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10 June 2020

Derralynn A Hughes

11

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10 June 2020

5

Roberto Giugliani

1 reference

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10 June 2020

17

Paul R Harmatz

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10 June 2020

Moeenaldeen D AlSayed

3

object named as

Moeenaldeen D AlSayed

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10 June 2020

4

Julian Raiman

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10 June 2020

9

Norberto Guelbert

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10 June 2020

10

Fiona Stewart

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10 June 2020

14

Robert Matousek

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10 June 2020

15

Elaina Jurecki

1 reference

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Martha L Solano Villarreal

10 June 2020

6

object named as

Martha L Solano Villarreal

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10 June 2020

author name string

Rossella Parini

2

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10 June 2020

Barbara K Burton

8

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10 June 2020

Peter Slasor

13

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10 June 2020

Adam J Shaywitz

16

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10 June 2020

publication date

16 June 2016

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http://europepmc.org/abstract/MED/27380995

9 April 2018

number of pages

13

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based on heuristic

inferred from page(s)

published in

Molecular Genetics and Metabolism

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10 June 2020

volume

119

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10 June 2020

page(s)

131-143

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10 June 2020

issue

1-2

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International guidelines for the management and treatment of Morquio A syndrome.

10 June 2020

cites work

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

The Morquio A Clinical Assessment Program: baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

Mucopolysaccharidosis type IVA (Morquio A disease): clinical review and current treatment

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

A systematic review of the prevalence of Morquio A syndrome: challenges for study reporting in rare diseases

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

Burden of disease in patients with Morquio A syndrome: results from an international patient-reported outcomes survey

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

Elosulfase alfa: first global approval

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

Multi-domain impact of elosufase alfa in Morquio A syndrome in the pivotal phase III trial

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

Longitudinal analysis of endurance and respiratory function from a natural history study of Morquio A syndrome.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

Immunogenicity of Elosulfase Alfa, an Enzyme Replacement Therapy in Patients With Morquio A Syndrome: Results From MOR-004, a Phase III Trial

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2016.05.018

10.1016/J.YMGME.2016.05.018

7 January 2021

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27380995%20AND%20SRC:MED&resulttype=core&format=json

10 June 2020

1 reference