Intravenous high-dose enzyme replacement therapy with recombinant palmitoyl-protein thioesterase reduces visceral lysosomal storage and modestly prolongs survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis (Q36240598)

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Intravenous high-dose enzyme replacement therapy with recombinant palmitoyl-protein thioesterase reduces visceral lysosomal storage and modestly prolongs survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis
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    Intravenous high-dose enzyme replacement therapy with recombinant palmitoyl-protein thioesterase reduces visceral lysosomal storage and modestly prolongs survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis (English)
    Jui-Yun Lu
    Andrew M S Wong
    Linda S Hynan
    Shari G Birnbaum
    Denis S Yilmaz
    Barbara M Streit
    Ewelina M Lenartowicz
    Thomas C M Thompson
    Jonathan D Cooper
    Sandra L Hofmann
    22 May 2012
    107
    213-221
    1-2

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